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2023 MDA Conference: Advances in Therapy for Mitochondrial Myopathies.
2023 MDA Conference: Periodic Paralysis and LGMD with a focus on the SCN4A and CACNA1S variants.
2023 MDA Conference: Inherited Neuropathies, Charcot Marie Tooth and TRPV4 Research
MDA Virtual Learning: Gene Therapy 101
MDA Advocacy Institute: Policies Influencing Gene Therapy Development 1
Mitochondrial medicine 2022 | Keynote talk | Carsten Bönnemann (National Institutes of Health, USA)
Rare Disease Day 2023 - Accelerating Rare Disease Research: Patients as Partners
Genetic Treatments: Recent Successes and Lessons for all NMD presented by John W. Day, MD, PhD.
Ask the Mito Doc: January 2023 - Conserving Your Energy in the New Year
Becker Breakout Session: Clinical Care -- PPMD 2023 Annual Conference
2023 FSHD Patient Day
Immune-Mediated Myopathies (Myositis/IBM) presented by Marie Beaudin, MD, MS.